Department of Hematology and Rare Diseases, V Cervello, Azienda Ospedaliera Ospedali Riuniti Villa Sofia-Cervello, Palermo, Italy. Electronic address: aurelio.maggio@villasofia.it. First Department of Pediatrics, National and Kapodistriam University of Athens, Athens, Greece. Consorzio per Valutazioni Biologiche e Farmacologiche, Bari-Pavia, Italy. Biostatistics and Data Management Unit, Medi Service, Genoa, Italy. Pediatric Hospital, Cairo University, Cairo, Egypt. Pediatrics and Bone Marrow Transplantation Centre, Tunis, Tunisia. Pediatrics Department, Faculty of Medicine, Zagazig University, Zagazig, Egypt. Thalassaemia Center, Hospital Archbishop Makarios III, Nicosia, Cyprus. Clinica Pediatrica, Azienda Ospedaliero Universitaria (AOU) Sassari, Sassari, Italy. Clinical Pharmacology and Therapeutics Group, University College London, London, UK. UO Pediatrica B Trambusti, AOU Consorziale Policlinico-Giovanni XXIII, Bari, Italy. UOSD Malattie rare del globulo rosso, AORN A Cardarelli, Napoli, Italy. UOC Ematologia con Talassemia, Dipartimento di Medicina, AO Civico Di Cristina-Benfratelli, Palermo, Italy. Department of Pediatrics and Clinical Research Center, Faculty of Medicine, Alexandria University, Alexandria, Egypt. Pediatrics Department, University Hospital Center Mother Teresa, Tirana, Albania. DH Talassemia, Ospedale Pediatrico Microcitemico A CAO, AO G Brotzu, Cagliari, Italy. Department of Women's and Child's Health (DSDB), University Hospital, Padova, Italy. ApoPharma, Toronto, ON, Canada. Centre for Genomics and Child Health, Blizard Institute, Queen Mary University of London, London, UK. Department of Hematology and Rare Diseases, V Cervello, Azienda Ospedaliera Ospedali Riuniti Villa Sofia-Cervello, Palermo, Italy. Center of Thalassemia, Hospital Ihsan Cabej, Lushnje, Albania. Fondazione per la Ricerca Farmacologica Gianni Benzi Onlus, Valenzano, Italy.